Exciting Autism Research: Hope for Rett and Dravet Syndromes
Recent scientific breakthroughs offer new hope for families affected by Rett and Dravet syndromes, both of which often co-occur with autism. Learn what these advancements mean for your family.
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For Dravet, a gene regulation therapy called zorevunersen is showing promise, with some patients experiencing significant seizure reductions, cognitive gains, and improved quality of life. You can find more information about the Emperor study, a Phase 3 trial for zorevunersen, at [https://www.emperorstudy.com/]....(https://www.emperor
In Rett syndrome, a gene-targeting strategy is showing potential in restoring brain function. Also, UCB is testing fintepla (already approved for Dravet) in Rett and CDKL5. The IRSF has a webinar with more details and slides available here: [https://www.youtube.com/watch?....v=HRqav2LwkxI](https and [https://www.rettsyndrome.org/w....p-content/uploads/20
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